| 2013 |
TRAPPC11 mutations (p.Gly980Arg in the gryzun domain and p.Ala372_Ser429del in the foie gras domain) impair binding of TRAPPC11 to other TRAPP complex components and disrupt Golgi apparatus architecture; the foie gras domain deletion causes normal ER-to-Golgi trafficking but dramatically delayed exit from the Golgi to the cell surface, and leads to alterations of lysosomal membrane glycoproteins LAMP1 and LAMP2. |
Co-immunoprecipitation, marker trafficking experiments, immunofluorescence of Golgi markers, western blotting of LAMP1/LAMP2 in patient fibroblasts with defined mutations |
American journal of human genetics |
High |
23830518
|
| 2016 |
TRAPPC11 is required for lipid-linked oligosaccharide (LLO) biosynthesis and protein N-glycosylation; depletion of TRAPPC11 (but not other TRAPP components) in human cells causes protein hypoglycosylation associated with reduced LLO levels and compensatory upregulation of the terpenoid/dolichol biosynthetic pathway, leading to a stressed unfolded protein response and lipid droplet accumulation. |
Zebrafish trappc11 mutant analysis, siRNA knockdown of TRAPPC11 in human cells, LLO level measurement, UPR reporter assays, pharmacological inhibition of terpenoid/LLO synthesis, patient fibroblast analysis |
Molecular biology of the cell |
High |
26912795
|
| 2016 |
A TRAPPC11 splice mutation (c.1893+3A>G) causes incomplete exon skipping, dramatic reduction of full-length TRAPPC11 protein, hypoglycosylation of LAMP1, delayed arrival of marker proteins at the Golgi, and delayed release from the Golgi to the plasma membrane in patient fibroblasts. |
Western blotting, membrane trafficking assays with fluorescent cargo markers in patient fibroblasts, mRNA analysis |
Journal of medical genetics |
Medium |
27707803
|
| 2015 |
TRAPPC11 is a component of the multiprotein TRAPP complex involved in endoplasmic reticulum-to-Golgi trafficking; loss of full-length TRAPPC11 protein (due to compound heterozygous mutations including a novel splice-site mutation causing frameshift/truncation) causes congenital muscular dystrophy with steatosis, demonstrating a physiological role in multiple tissues. |
Immunoblotting showing absence of full-length TRAPPC11, mRNA splicing analysis, muscle and liver biopsy histology |
Skeletal muscle |
Medium |
26322222
|
| 2018 |
TRAPPC11 mutations are associated with hypoglycosylation of α-dystroglycan; compound heterozygous TRAPPC11 mutations (c.851A>C and c.965+5G>T) cause abnormal membrane trafficking in patient fibroblasts, linking membrane trafficking defects to dystroglycanopathy for the first time. |
Immunofluorescence and western blotting for α-dystroglycan glycosylation, live cell membrane trafficking analysis in patient fibroblasts |
Skeletal muscle |
Medium |
29855340
|
| 2019 |
TRAPPC11 functions in membrane trafficking and autophagy as a component of TRAPP III; variants affecting the carboxy terminus (frameshift p.Asp1127Valfs*47) cause defects in ER-to-Golgi transport, Golgi exit, and glycosylation of an ER-resident glycoprotein, while the compound heterozygous (foie gras deletion + C-terminal frameshift) combination additionally causes autophagic flux defects not seen with the missense variant alone, highlighting the critical role of the extreme carboxy terminus. |
Membrane trafficking assays, glycosylation assays (ER-resident glycoprotein), autophagic flux assay in patient fibroblasts with defined bi-allelic variants |
Scientific reports |
Medium |
31575891
|
| 2021 |
TRAPPC11 is important for complex integrity and anterograde membrane transport from the ER to the ER-Golgi intermediate compartment; mutations cause universal hypoglycosylation of α-dystroglycan in skeletal muscle and brain (including Purkinje cells and dentate neurons), with neuropathology resembling N-linked congenital disorders of glycosylation. |
Membrane trafficking assays in patient fibroblasts, immunofluorescence with IIH6 antibody for α-dystroglycan glycosylation in muscle and post-mortem brain, neuropathological examination |
Neuropathology and applied neurobiology |
Medium |
34648194
|
| 2023 |
TRAPPC11 deficiency impairs mitochondrial function: patient fibroblasts/muscle from individuals with the c.1287+5G>A founder variant show decreased mitochondrial ATP production capacity and alterations in mitochondrial network architecture. |
Mitochondrial ATP production assays and mitochondrial network morphology analysis in patient-derived cells |
Journal of medical genetics |
Low |
37197784
|
| 2024 |
TRAPPC11 mutations cause defective ER-to-Golgi transport and decreased expression of LAMP2 and ICAM-1 glycoproteins, further supporting TRAPPC11-opathy as a congenital disorder of glycosylation (CDG) with muscular dystrophy. |
Membrane trafficking assays and western blotting for glycoprotein expression in patient fibroblasts |
Molecular genetics and metabolism |
Medium |
38564972
|